Is Zofran (ondansetron) safe to take during pregnancy?

Comment by InpharmD Researcher

According to the package insert, published epidemiological studies on the association between ondansetron use during pregnancy and major birth defects have reported inconsistent findings and have important methodological limitations that preclude conclusions about the safety of ondansetron use in pregnancy. Additionally, postmarketing data have not identified a drug-associated risk of miscarriage or adverse maternal outcomes. Societal guidelines and expert opinions dictate the use of ondansetron to be second- or third-line, given the scarcity of direct comparison data. Recent meta-analyses, primarily based on observational studies or administrative databases, generally report a nonsignificant association between the use of ondansetron and major congenital malformations. Exposure to ondansetron during the first trimester of pregnancy has been reported with increased risks of ventricular septal defects and orofacial clefts, although this data is conflicting. As most pooled analyses lack consistent information on dosing regimens and duration of exposure, findings should be interpreted with caution.

Background

The American College of Obstetrics and Gynecology (ACOG) discussed antiemetic options for pregnancy in a 2018 practice bulletin. Overall, no single therapeutic approach has proven most effective for pregnancy or each of the three stages, and risk and benefits should be weighed on a case-by-case basis. The recommended algorithm for general pregnancy-related nausea and vomiting recommends a stepwise approach. Vitamin B6 (pyridoxine) with/without doxylamine is initially recommended. If symptoms persist, the addition of dimenhydrinate PRN/scheduled dosing, prochlorperazine, or promethazine is recommended. The continuation of symptoms leads to the addition of other agents depending on the hydration status of patients (no dehydration: oral ondansetron; dehydration: intravenous ondansetron; see Table 1). [1]

A 2022 systematic review and meta-analysis evaluated abnormal pregnancy outcomes after using ondansetron during pregnancy. In total, 20 articles were analyzed, which consisted of 11 cohort studies, 5 case-control studies, 2 case reports, and 1 case series. Compared with patients who did not use ondansetron, patients who were exposed reported higher incidence of cardiac defects (odds ratio [OR] 1.06; 9% confidence interval [CI] 1.01 to 1.10), neural tube defects (OR 1.12; 95% CI 1.05 to 1.18), and chest cleft (OR 1.21; 95% CI 1.07 to 1.37), although a later sensitivity analysis showed no difference between groups regarding incidence of cardiac defects or neural tube defects, and elimination of controversial studies resulted in no association found between ondansetron and cardiac defects altogether. An association between ondansetron and reduced incidence of miscarriage was observed (OR 0.53; 95% CI 0.31 to 0.89). No difference between groups was found in incidence of orofacial clefts, spinal limb defects, urinary tract deformities, any congenital malformations, stillbirth, preterm birth, neonatal asphyxia, or neonatal development. Notably, duration of treatment and dosage varied between cases, and ondansetron was often reserved for patients with more severe symptoms per societal guidelines, thus introducing confounding within the results. [2]

A 2020 network meta-analysis (NMA) of 18 randomized controlled trials (RCTs) compared different treatment options including promethazine in pregnant individuals with hyperemesis gravidarum (HG). The primary outcome of control of HG symptoms did not include promethazine in the analysis (n= 400 participants), demonstrating methylprednisolone (OR 6.7; 95% CI 1.1 to 38.8) as the only pharmacological intervention to be associated with significantly better control of HG symptoms compared to standard of care. For secondary outcomes, ondansetron was associated with reduced hospital stay (weighted mean difference [WMD] -0.2; 95% CI -0.31 to -0.01) and diazepam with reduced risk of hospital admission (OR 0.11; 95% CI 0.01 to 0.95). Compared to metoclopramide, promethazine did not exhibit significantly better improvements in emetic episodes, nausea scores, hospital stay, and quality of life. Similarly, no significant differences were noted between promethazine and the standard of care in the use of rescue antiemetics and hospital admission. Subgroup analysis of patients with severe nausea/vomiting associated with dehydration and metabolic disturbances in the form of ketonuria and weight loss found no differences in the primary outcomes between methylprednisolone and ondansetron compared to metoclopramide. The overall quality of evidence appeared to be very low, and findings need to be confirmed in head-to-head clinical trials in the future. [3]

A 2017 book chapter from the Emergency Department Management of Obstetric Complications provided a stepwise treatment approach to managing pregnancy-associated nausea and vomiting. Similar to the guideline recommendations, pyridoxine plus doxylamine is recommended as the first-line pharmacological intervention in addition to supportive care. Second-line options for relieving moderate to severe vomiting included diphenhydramine, dimenhydrinate, or metoclopramide. In patients with refractory symptoms not responding to aforementioned second-line agents, ondansetron, prochlorperazine, promethazine, or methylprednisolone may be administered. Additionally, promethazine suppository is another option for patients unable to tolerate oral medications. Though not directly compared with each other, higher quality evidence existed within medical literature for ondansetron compared to promethazine or prochlorperazine. It should be noted that steroids in general should be considered last resort therapy due to the risks of fetal oral clefts and low birth weight. [4]

A 2014 review on the outpatient management and special considerations of nausea and vomiting in pregnancy (NVP) assessed the conservative measures and available pharmacotherapy for the treatment of the symptoms of nausea and vomiting despite changes in lifestyle and nutrition. The combination of oral pyridoxine and doxylamine for the treatment of NVP has the most data on safety and efficacy and has been utilized by healthcare providers in the U.S. Dimenhydrinate and promethazine were considered second-line agents for NVP that can be administered orally or rectally. Human and animal studies did not demonstrate an association between the use of promethazine during pregnancy (including the first trimester) and an increased risk of malformation. If none of the previously mentioned medications control symptoms, the third-line therapy for NVP would be changing the route of delivery of promethazine to intramuscular. Metoclopramide is another medication that can be given orally or intramuscularly. Metoclopramide works as an antiemetic and prokinetic agent by decreasing gastrointestinal emptying time and acting on the chemoreceptor trigger zone. Therefore, it can be useful in patients with diabetes and gastroesophageal reflux disease. If symptoms are still not adequately controlled, a serotonin 5-hydroxytryptamine 3-receptor (5-HT3) antagonist such as ondansetron can be introduced. While ACOG guidelines reserve the use of ondansetron as a last-line therapy for NVP in the presence of dehydration, it is often prescribed in the outpatient setting due to less sedating effects when compared to promethazine and antihistamine. As every woman has her perception of disease severity and desire for treatment, it is essential to track symptoms in order to assess for a decrease or resolution of symptoms as well as escalations in symptoms that might require additional therapy. [5]

A 2022 study on birth defects using data from the case-control National Birth Defects Prevention Study (1997-2011) to examine whether first-trimester NVP or its specific treatments were associated with 37 major birth defects. Overall, mothers of 66.6% of 28,628 cases and 69.9% of 11,083 controls reported first-trimester NVP. Pooled analysis demonstrated increased risks for promethazine and tetralogy of Fallot (adjusted OR [aOR] 1.49; 95% CI 1.05 to 2.10), promethazine and craniosynostosis (aOR 1.44; 95% CI 1.08 to 1.92), ondansetron and cleft palate (aOR 1.66; 95% CI 1.18 to 2.31), pyridoxine and heterotaxy (aOR 3.91; 95% CI 1.49 to 10.27), and pyridoxine and cataracts (aOR 2.57; 95% CI 1.12 to 5.88). Notably, findings do not necessitate causation, as data were derived from reports of first-trimester NVP. [6]

References:

[1] Committee on Practice Bulletins-Obstetrics. ACOG Practice Bulletin No. 189: Nausea And Vomiting Of Pregnancy. Obstet Gynecol. 2018;131(1):e15-e30. doi:10.1097/AOG.0000000000002456
[2] Cao X, Sun M, Yang Q, et al. Risk of abnormal pregnancy outcomes after using ondansetron during pregnancy: A systematic review and meta-analysis. Front Pharmacol. 2022;13:951072. Published 2022 Sep 2. doi:10.3389/fphar.2022.951072
[3] Sridharan K, Sivaramakrishnan G. Interventions for treating hyperemesis gravidarum: a network meta-analysis of randomized clinical trials. J Matern Fetal Neonatal Med. 2020;33(8):1405-1411. doi:10.1080/14767058.2018.1519540
[4] DeGeorge, L., Wiesner, L. (2017). Approach to the Patient with Nausea and Vomiting in Pregnancy. In: Borhart, J. (eds) Emergency Department Management of Obstetric Complications. Springer, Cham. https://doi.org/10.1007/978-3-319-54410-6_3
[5] Clark SM, Dutta E, Hankins GD. The outpatient management and special considerations of nausea and vomiting in pregnancy. Semin Perinatol. 2014;38(8):496-502. doi:10.1053/j.semperi.2014.08.014
[6] Schrager NL, Parker SE, Werler MM, For The National Birth Defects Prevention Study. The association of nausea and vomiting of pregnancy, its treatments, and select birth defects: Findings from the National Birth Defect Prevention Study [published online ahead of print, 2022 Sep 27]. Birth Defects Res. 2022;10.1002/bdr2.2096. doi:10.1002/bdr2.2096

Relevant Prescribing Information

Published epidemiological studies on the association between ondansetron use and major birth defects have reported inconsistent findings and have important methodological limitations that preclude conclusions about the safety of ondansetron use in pregnancy. Available postmarketing data have not identified a drug-associated risk of miscarriage or adverse maternal outcomes. Reproductive studies in rats and rabbits did not show evidence of harm to the fetus when ondansetron was administered during organogenesis at approximately 6 and 24 times the maximum recommended human oral dose of 24 mg/day, based on body surface area (BSA), respectively. [7]

References:

[7] Ondansetron tablet. Prescribing information. Aurobindo Pharma Limited; 2023.

Literature Review

A search of the published medical literature revealed 2 studies investigating the researchable question:

Is Zofran (ondansetron) safe to take during pregnancy?

Level of evidence

C - Multiple studies with limitations or conflicting results  Read more→



Please see Tables 1-2 for your response.


 

Ondansetron Use During Pregnancy: Birth Defects and Obstetric Outcomes

Design

Retrospective cohort study

N= 1,548

Objective

To investigate whether exposure to ondansetron during pregnancy was associated with an increased risk of adverse obstetric and/or fetal outcomes, including congenital heart defects (CHD) and other major birth defects, preterm delivery, small for gestational age (SGA), or stillbirth

Study Groups

Control (n= 774)

Ondansetron (n= 774)

Inclusion Criteria

Women with NVP treated with ondansetron; pregnant women without NVP not treated with ondansetron

Exclusion Criteria

Aged <18 or >40 years; concomitant illness requiring chronic medication treatment; chronic alcohol consumption during pregnancy; treatment with ondansetron <1 month

Methods

Data were collected from computerized databases on pregnant women and their newborns; a matched-control stratum was utilized at a 1:1 ratio using a nearest-neighbor approach. Ondansetron was prescribed at a daily dose of 4 or 8 mg, for more than four weeks. No concomitant chronic medications were prescribed.

Duration

Between 2012 and 2016

Outcome Measures

Birth defects, SGA, preterm birth, stillbirth

Baseline Characteristics

 

Control (n= 774)

Ondansetron (n= 774)

 

Age, years

29.40 ± 4.81 29.53 ± 4.88  

Body mass index, kg/m2

24.67 ± 2.87 24.58 ± 2.93  

Parity

0.86 ± 1.05 0.88 ± 1.04  

Gestational age at delivery, weeks

38.82 ± 1.36 38.78 ± 1.62  

Birth weight, g

3,148.54 ± 509.23 3,172.29 ± 494.53  

No maternal cigarette smoking

684 (88.4%) 690 (89.1%)  

Results

Endpoint

Control (n= 774)

Ondansetron (n= 774)

p-value

Congenital abnormalities

Cleft lip and/or palate

Cardiac defect (VSD)

Neural tube defects

 

0

1.3%

0

 

0

0.5%

0

 

1.0

0.18

1.0

Preterm delivery <37 weeks

5.29% 5% 0.739

Small for gestational age

4% 5% 0.328

Abbreviations: VSD= ventricular septal defect

Adverse Events

See Results

Study Author Conclusions

The findings of the present study suggest that maternal exposure to ondansetron during pregnancy may not be associated with fetal congenital malformations. No increased risk of birth defects or other adverse fetal and maternal outcomes were found. Ondansetron may be a useful and safe alternative as a treatment for women who suffer from HG who do not respond to other antiemetic medications. Notwithstanding, future large-scale prospectively designed studies are needed to determine the teratogenic capacity of ondansetron.

InpharmD Researcher Critique

Due to the retrospective, observational nature of the data, findings may be misclassified or missing, and use of a small sample size in each group limits applicability to a broader population. Additionally, dosing schedule, use of over-the-counter medications or supplements, and stratification of exposure by trimester was not provided to further analyze.

References:

Masarwe S, Shvartsur R, Hadar E, Betesh-Abay B, Peleg N, Azab AN. Ondansetron Use During Pregnancy: Birth Defects and Obstetric Outcomes. Clin Nurs Res. 2023;32(4):705-711. doi:10.1177/10547738231159062

 

Algorithm of Therapeutic Treatment of Nausea and Vomiting of Pregnancy

First-Line Therapy: Nonpharmacologic options

Convert prenatal vitamins to folic acid supplements only
Ginger capsules 250 mg four times daily
Consider P6 acupressure with wristbands

Persistent symptoms 

Pharmacologic Options*
Vitamin B6 (pyridoxine) 10–25 mg orally (either taken alone or in combination with doxylamine† 12.5 mg orally), 3 or 4 times per day. Adjust schedule and dose according to the severity of patient’s symptoms.
OR
Vitamin B6 (pyridoxine) 10 mg/Doxylamine 10 mg combination product, two tablets orally at bedtime initially, up to four tablets per day (one tablet in the morning, one tablet in mid-afternoon, and two tablets at bedtime)

OR
Vitamin B6 (pyridoxine) 20 mg/Doxylamine 20 mg combination product, one tablet orally at bedtime initially, up to two tablets per day (one tablet in the morning and one tablet at bedtime)

Persistent symptoms 

 Add the following:

(presented here in alphabetical order)
Dimenhydrinate, 25–50 mg every 4–6 hours, orally as needed (not to exceed 200 mg per day if patient also is taking doxylamine)

OR
Diphenhydramine, 25–50 mg orally every 4–6 hours
OR
Prochlorperazine, 25 mg every 12 hours rectally
OR
Promethazine, 12.5–25 mg every 4–6 hours, orally or rectally

No dehydration

Dehydration

Intravenous fluid replacement‡ 

↓ 

Persistent symptoms

Add any of the following:
(presented here in alphabetical order)
Metoclopramide, 5–10 mg every 6–8 hours, orally or intramuscularly
OR
Ondansetron, 4 mg orally every 8 hours
OR
Promethazine, 12.5–25 mg every 4–6 hours, orally, rectally, or intramuscularly
OR
Trimethobenzamide, 200 mg every 6–8 hours, intramuscularly

 

 

 

↓ 

Persistent symptoms

Add any of the following:
(presented here in alphabetical order)
Dimenhydrinate, 50 mg (in 50 mL saline, over 20 min) every 4–6 hours, intravenously
OR
Metoclopramide, 5–10 mg every 8 hours, intravenously
OR
Ondansetron, 8 mg, over 15 minutes, every 12 hours, intravenously
OR
Promethazine, 12.5–25 mg every 4–6 hours, intravenously

↓ 

Persistent symptoms

Add the following:
(presented here in alphabetical order)
Chlorpromazine 25–50 mg intravenously or intramuscularly every 4–6 hours or 10–25 mg orally every 4 to 6 hours.
OR
Methylprednisolone 16 mg every 8 hours, orally or intravenously,
for 3 days. Taper over 2 weeks to the lowest effective dose. If beneficial, limit the total duration of use to 6 weeks.

This algorithm assumes other causes of nausea and vomiting have been ruled out. At any step, consider enteral nutrition if dehydration or persistent weight loss is noted. *Some antiemetic medications have only been approved by the U.S. Food and Drug Administration for use in nonpregnant patients; however, off-label use is common. Obstetricians and other obstetric care providers should counsel patients and document such discussions accordingly. Care should be exercised if multiple antiemetic medications are used simultaneously. Parallel use of some†medications (see text) may result in an increased risk of adverse effects. In the United States, doxylamine is available as the active ingredient in some over-the-counter sleep aids; one-half of a scored 25-mg tablet can be used to provide a 12.5-mg dose of doxylamine. ‡Thiamine, intravenously, 100 mg with the initial rehydration fluid and 100 mg daily for the next 2–3 days (followed by intravenous multivitamins), is recommended for women who require intravenous hydration and have vomited for more than 3 weeks to prevent a rare but serious maternal complication, Wernicke encephalopathy. (Modified from Levichek Z, Atanackovic G, Oepkes D, Maltepe C, Einarson A, Magee L, et al. Nausea and vomiting of pregnancy. Evidence-based treatment algorithm.)

 

References:

Adapted from:
Committee on Practice Bulletins-Obstetrics. ACOG Practice Bulletin No. 189: Nausea And Vomiting Of Pregnancy. Obstet Gynecol. 2018;131(1):e15-e30. doi:10.1097/AOG.0000000000002456